Spotlight: New Gene Therapies on the Horizon for the Treatment of Neurogenetic Diseases
Gene therapies have dramatically altered the landscape of neurological disease treatments, with the USFDA expecting to review 10 to 20 cell and gene therapies each year by 2025. Over 1000 gene therapy studies are currently underway for neurological diseases. Here, we attempted to review the field.
Although the genetic basis underlying common neurological and neuromuscular disorders