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Duchenne Muscular Dystrophy-dmd
Trials & Approvals Duchenne Muscular Dystrophy-dmdOrphan Drug Designation
The U.S. FDA Grants Orphan Drug Designation to NS-089/NCNP-02 for the Treatment of DMD
2023-08-17
Trials & Approvals Duchenne Muscular Dystrophy-dmd
Entrada Hit With Clinical Hold on IND Application for Muscular Dystrophy Therapy
2022-12-20
Trials & Approvals Duchenne Muscular Dystrophy-dmd
Sarepta Submits BLA for First-Ever Duchenne Muscular Dystrophy Gene Therapy
2022-10-03
Trials & Approvals Orphan Drug
The FDA Granted These Three Companies Orphan Drug Designations in One Day
2022-05-13
Special Gene Therapy
Harnessing Viral Evolution to Deliver Gene Therapy to Specific Tissues
2021-09-13
Trials & Approvals Gene Therapy
Sarepta to Begin Phase 3 Rivalry with Pfizer after its DMD Gene Therapy Registers Encouraging Data
2021-05-21
Trials & Approvals Gene Therapy
Sarepta’s Stocks Drop 50% Following Middling Trial Data for Gene Therapy
2021-01-11
Technology CRISPR
Eli Lilly Forays into Gene Editing with Precision BioSciences Collaboration
2020-11-21
Technology
The Future of CRISPR: Three Areas The Nobel Prize Winning Tech Will Be Most Impactful
2020-10-25
Funding Dual Amine Oxidase Inhibitor
Australian Pharma Bags Government Funding to Fight Duchenne Muscular Dystrophy
2020-09-06
R&D
Altering the Treatment Landscape of Neurodegenerative Diseases Using Antisense Oligonucleotides (ASOs)
2020-08-17
In-Depth
Spotlight: New Gene Therapies on the Horizon for the Treatment of Neurogenetic Diseases
2020-08-03
Technology CRISPR
Scientists Use CRISPR To Fight Duchenne Muscular Dystrophy
2020-01-29
Today In History CRISPR
December 31, 2015: Researchers First Used CRISPR to Treat a Genetic Disease in Mice
2017-12-31
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