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Orphan Drug Designation
Trials & Approvals Duchenne Muscular Dystrophy-dmdOrphan Drug Designation
The U.S. FDA Grants Orphan Drug Designation to NS-089/NCNP-02 for the Treatment of DMD
2023-08-17
Trials & Approvals IgA NephropathySouth Korea
South Korea Puts Everest Medicines’ Nefecon On Fast Track
2023-02-10
Trials & Approvals Orphan Drug Designation
Algernon Wins FDA Orphan Drug Designation For Rare Lung Disease Candidate
2022-12-07
Trials & Approvals IgA Nephropathy
Everest’s Renal Drug Gets Placed On Fast Track For Approval In Taiwan And Korea
2022-11-28
Trials & Approvals Orphan Drug
BioCryst’s ALK-2 Inhibitor Granted FDA Orphan Drug Status For Rare Bone Disease
2022-09-01
Trials & Approvals Orphan Drug Designation
Three Companies Received Orphan Drug Designations in One Day To Treat Rare Cancers
2022-06-20
Trials & Approvals Orphan Drug
Telix Granted FDA Orphan Drug Designation for Bone Marrow Conditioning Treatment
2022-03-29
Asia-Pacific Orphan Drug Designation
GC Pharma’s Enzyme Replacement Therapy Wins Orphan Drug Designation from EMA
2021-11-02
R&D
BARDA Funds Development of Live Biotherapeutic Product Against C. difficile Infections
2020-10-05
COVID-19 Orphan Drug Designation
Gilead Requests FDA to Rescind Remdesivir’s Orphan Drug Designation
2020-03-25
COVID-19 Orphan Drug Designation
Gilead’s Remdesivir Wins FDA’s Orphan Drug Designation for COVID-19 Treatment
2020-03-24
R&D ATP7B Gene
Pfizer Collaborates with Vivet to Develop Gene Therapy for Wilson Disease
2019-03-29
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