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Orphan Drug
Ocelot’s Rare Kidney Disease Candidate Receives Orphan Drug Designation Going Into Phase 2 Trials
2022-08-23
Three Companies Received Orphan Drug Designations in One Day To Treat Rare Cancers
2022-06-20
The FDA Granted These Three Companies Orphan Drug Designations in One Day
2022-05-13
Telix Granted FDA Orphan Drug Designation for Bone Marrow Conditioning Treatment
2022-03-29
Applied Therapeutics’ Galactosemia Program Stumbles Again after FDA Requests for More Data
2022-01-04
FDA Greenlights Eton and Diurnal’s Orphan Drug for Pediatric Patients
2020-10-04
Investigational Gene Therapy for Cystinosis Obtains FDA’s Orphan Drug Designation
2020-03-10
Weekly in Asia|Nov-2
2019-11-27
Sangamo’s Shares Goes up after the Announcement of Investigational Hemophilia A Gene Therapy Results
2019-07-19
LATEST
SK Biopharma and Full-Life Sign US$571.5 Million Deal for Innovative Radiopharmaceutical FL-091
2024-07-18
Autoimmune Patients See Breakthrough Response to Allogeneic CD19-Targeted CAR-T Therapy
2024-07-18
Rising Bird Flu Cases in Cattle and Humans Drive Global Efforts in Vaccination, Genetic Monitoring, and Surveillance
2024-07-17
STLI Webinar Series 1: Experts Discuss Regulatory Trends in Regenerative Medicine
2024-07-16
Wistar and Accelerated Biosciences Partner to Develop Novel hTSCs Platform for Immunotherapies
2024-07-15
Accelerated Bio and Pluristyx Generate Clinical-Grade Induced Pluripotent Stem Cells from Reprogrammed Human Trophoblast Stem Cells
2024-07-12
Novo Nordisk and PT Bio Farma Agree to Enhance Insulin Production for Diabetes Patients in Indonesia
2024-07-12
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