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Orphan Drug
Ocelot’s Rare Kidney Disease Candidate Receives Orphan Drug Designation Going Into Phase 2 Trials
2022-08-23
Three Companies Received Orphan Drug Designations in One Day To Treat Rare Cancers
2022-06-20
The FDA Granted These Three Companies Orphan Drug Designations in One Day
2022-05-13
Telix Granted FDA Orphan Drug Designation for Bone Marrow Conditioning Treatment
2022-03-29
Applied Therapeutics’ Galactosemia Program Stumbles Again after FDA Requests for More Data
2022-01-04
FDA Greenlights Eton and Diurnal’s Orphan Drug for Pediatric Patients
2020-10-04
Investigational Gene Therapy for Cystinosis Obtains FDA’s Orphan Drug Designation
2020-03-10
Weekly in Asia|Nov-2
2019-11-27
Sangamo’s Shares Goes up after the Announcement of Investigational Hemophilia A Gene Therapy Results
2019-07-19
LATEST
Previewing AACR 2024 With Select Pre-Meeting Highlights
2024-03-28
Roche Delivering on Malaria Screening Solutions for Blood Donation
2024-03-28
Innovating Cancer Treatment: The Role of ADC Technology at Nona Biosciences
2024-03-28
BIO CHINA 2024 Brings Biotech Experts and Industry Elites Together for Innovation
2024-03-27
Galderma’s Strong European IPO Debut
2024-03-26
Markets and Mergers: Boston Scientific and Axonics Shake Hands on Deal
2024-03-25
Discover the Next Billion-Dollar Unicorn at the Biotech Innovation Funding Networking Event
2024-03-21
EVENT
2024-04-06
Biotech Innovation Funding Networking
Los Angeles, USA
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