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Rare Disease
ASCO 2024 ASCO 2024US BIO
Merck Buys EyeBio for $3B and Shares Global Policy Perspectives During BIO in San Diego
2024-06-20
Trials & Approvals Gene TherapyRare Disease
Orchard Therapeutics’ Gene Therapy for Rare Neurological Disorder Wins FDA Approval
2024-03-20
Partnerships Novo NordiskTargeted Protein Degradation
Neomorph Links Together With Novo Nordisk in a $1.46 Billion Molecular Glue Partnership Deal
2024-02-27
Funding Pompe diseaseRare Disease
Amicus Therapeutics Secures $430 Million Financing Pact with Blackstone to Propel Rare Disease Mission
2023-10-04
Trials & Approvals FDA Approval
FDA Approves First Treatment for Fibrodysplasia Ossificans Progressiva
2023-08-21
Trials & Approvals Duchenne Muscular Dystrophy-dmdOrphan Drug Designation
The U.S. FDA Grants Orphan Drug Designation to NS-089/NCNP-02 for the Treatment of DMD
2023-08-17
Trials & Approvals Rare Disease
Reata’s Groundbreaking Therapy for an Ultra-rare Neuromuscular Disease Secures FDA Approval
2023-03-02
Special biopharmam&a
GeneOnline’s Pick: Top 10 M&A Deals in 2022
2022-12-28
Trials & Approvals Rare Disease
AstraZeneca’s Treatment for Rare Throat Disease, Eosinophilic esophagitis, Fails Primary Endpoint
2022-10-25
Trials & Approvals Rare Disease
Bristol Myers Squibb’ sNDA for Rare Heart Disease Treatment Accepted by the FDA
2022-10-21
Funding FDA
Nineteen Grants and Two Contracts Grab $38 Million In Support From the FDA
2022-10-17
Trials & Approvals Albireo
Albireo Signals To Apply For FDA Approval After Trial Win
2022-10-12
Trials & Approvals AstraZeneca
AstraZeneca’s Rare Disease Treatment Wins Third Approval in European Union
2022-09-23
Trials & Approvals BridgeBio Pharma
BridgeBio and Sentynl Therapeutics’ Nulibry Gets Greenlighted In Europe
2022-09-21
Trials & Approvals Rare Disease
QOL Medical’s Sucraid Single-Use Containers Approved For Patients With Sucrase Deficiency
2022-09-07
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LATEST
AI-Based Model Accurately Classifies Pediatric Sarcomas Using Digital Pathology Images
2025-04-30
Taiwan’s BPIPO and DCB Join Japan’s LINK-J and FIRM for First Regenerative Medicine Investment Forum in Tokyo
2025-04-29
Study Shows ctDNA Liquid Biopsy Detects Colorectal Cancer Recurrence Earlier Than Imaging
2025-04-29
AACR Annual Meeting 2025: Cancer Research Innovations, NIH Funding Advocacy, and AI-Driven Advances
2025-04-28
Senti Biosciences to Showcase New Cell & Gene Therapy Data at AACR Annual Meeting 2025
2025-04-27
World Vaccine Congress Washington 2025 Recap: Urgent Calls for Trust, Tech, and Global Access
2025-04-25
Astellas’ Transformation Journey: From Merger to Global Player, Betting on the Edge of Innovation and Risk?
2025-04-25
READ MORE
EVENT
2025-04-25
AACR Annual Meeting 2025
Chicago, U.S.A
2025-05-03
29th Taiwan Joint Cancer Conference 2025
Taipei, Taiwan
2025-05-05
Swiss Biotech Day 2025
Basel, Switzerland
2025-05-13
ASGCT 28th Annual Meeting 2025
New Orleans, U.S.A.
2025-05-30
ASCO Annual Meeting 2025
Chicago, U.S.A
2025-06-11
ISSCR 2025 Annual Meeting
Hong Kong
SEE MORE
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