GENE ONLINE|News &
Opinion
Blog

Rare Disease
Funding Pompe diseaseRare Disease
Amicus Therapeutics Secures $430 Million Financing Pact with Blackstone to Propel Rare Disease Mission
2023-10-04
Trials & Approvals FDA Approval
FDA Approves First Treatment for Fibrodysplasia Ossificans Progressiva
2023-08-21
Trials & Approvals Duchenne Muscular Dystrophy-dmdOrphan Drug Designation
The U.S. FDA Grants Orphan Drug Designation to NS-089/NCNP-02 for the Treatment of DMD
2023-08-17
Trials & Approvals Rare Disease
Reata’s Groundbreaking Therapy for an Ultra-rare Neuromuscular Disease Secures FDA Approval
2023-03-02
Special biopharma
GeneOnline’s Pick: Top 10 M&A Deals in 2022
2022-12-28
Trials & Approvals Rare Disease
AstraZeneca’s Treatment for Rare Throat Disease, Eosinophilic esophagitis, Fails Primary Endpoint
2022-10-25
Trials & Approvals Rare Disease
Bristol Myers Squibb’ sNDA for Rare Heart Disease Treatment Accepted by the FDA
2022-10-21
Funding FDA
Nineteen Grants and Two Contracts Grab $38 Million In Support From the FDA
2022-10-17
Trials & Approvals Albireo
Albireo Signals To Apply For FDA Approval After Trial Win
2022-10-12
Trials & Approvals AstraZeneca
AstraZeneca’s Rare Disease Treatment Wins Third Approval in European Union
2022-09-23
Trials & Approvals BridgeBio Pharma
BridgeBio and Sentynl Therapeutics’ Nulibry Gets Greenlighted In Europe
2022-09-21
Trials & Approvals Rare Disease
QOL Medical’s Sucraid Single-Use Containers Approved For Patients With Sucrase Deficiency
2022-09-07
Trials & Approvals Orphan Drug
BioCryst’s ALK-2 Inhibitor Granted FDA Orphan Drug Status For Rare Bone Disease
2022-09-01
Trials & Approvals Sanofi
Sanofi’s Rare Disease Drug Granted First-Ever FDA Approval for the Condition
2022-09-01
Trials & Approvals Kidney Disease
Everest, Calliditas Win First Approval for Rare Kidney Disease Drug in Europe
2022-07-18
1 2 3 4
LATEST
BIODND – An AI-Powered Database That Breaks New Ground in Life Science Business Development
2023-11-29
GeneOnline’s Weekly News Highlights: Nov 20-Nov 24
2023-11-27
SK Bioscience and Hilleman Laboratories Join Forces for Ebola Vaccine Development
2023-11-23
BeiGene to Expand Oncology Pipeline Through ENSEM Therapeutics Partnership
2023-11-23
Advancing the Frontiers of Cell and Gene Therapy – An Interview with Dr. Shin Kawamata
2023-11-21
Astellas and Pfizer’s Drug Receives FDA Approval as Treatment for High-Risk Prostate Cancer Recurrence
2023-11-21
GeneOnline’s Weekly News Highlights: Nov 13-Nov 17
2023-11-20
READ MORE
EVENT
2023-11-30
2023 Healthcare+ EXPO・Taiwan
Taipei , Taiwan
SEE MORE
Newsletter

Subscribe to receive updates.

SIGN UP
Facebook
Youtube
Twitter
Linkedin
About
Explore
More
© 2023 GeneOnline
Privacy Policy | Terms of Service
Privacy Policy | Terms of Service
  • Subscribe to our newsletter and dive into the world of biopharma with us.
SIGN UP
x
Scroll to Top