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Rare Pediatric Disease
AVROBIO’s First-of-its-Kind Gene Therapy Receives Rare Pediatric Disease Designation
2022-09-21
Applied Therapeutics’ Galactosemia Program Stumbles Again after FDA Requests for More Data
2022-01-04
Retrophin Acquires Orphan Technologies to Develop Potential, Effective Cure for Rare Disease
2020-10-25
Potential Treatment for Osteogenesis Imperfecta Receives FDA’s “Rare Pediatric Disease Designation”
2020-09-27
LATEST
Innovative Cellular Mapping of BRCA-Related Breast Cancer Findings Reveals Novel Therapeutic Targets
2024-03-29
Previewing AACR 2024 With Select Pre-Meeting Highlights
2024-03-28
Roche Delivering on Malaria Screening Solutions for Blood Donation
2024-03-28
Innovating Cancer Treatment: The Role of ADC Technology at Nona Biosciences
2024-03-28
BIO CHINA 2024 Brings Biotech Experts and Industry Elites Together for Innovation
2024-03-27
Galderma’s Strong European IPO Debut
2024-03-26
Markets and Mergers: Boston Scientific and Axonics Shake Hands on Deal
2024-03-25
EVENT
2024-04-06
Biotech Innovation Funding Networking
Los Angeles, USA
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